Congenital aplastic anemia (Diamond Blackfan anemia)
Showing 1 - 25 of 4,015
Cancer in Inherited Bone Marrow Failure Syndromes
Recruiting
- Diamond Blackfan Anemia
- +4 more
-
Bethesda, Maryland
- +1 more
Jan 24, 2023
Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive, Acute Leukemia in Remission, Acute Lymphoblastic Leukemia
Active, not recruiting
- Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive
- +36 more
- Cyclophosphamide
- +4 more
-
Buffalo, New YorkRoswell Park Cancer Institute
Jan 23, 2023
Steroid-refractory Diamond-Blackfan Anemia (DBA) Trial run by the National Heart, Lung, and Blood Institute (NHLBI) (Bitopertin)
Not yet recruiting
- Steroid-refractory Diamond-Blackfan Anemia (DBA)
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Apr 28, 2023
Diamond Blackfan Anemia, Pure Red Cell Aplasia Trial in Boston, Manhasset (Trifluoperazine)
Terminated
- Diamond Blackfan Anemia
- Pure Red Cell Aplasia
-
Boston, Massachusetts
- +1 more
Nov 18, 2022
Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Adrenoleukodystrophy Trial in Denver, Valhalla, Salt Lake City (Human
Completed
- Mucopolysaccharidosis I
- +15 more
- Human Placental Derived Stem Cell
-
Denver, Colorado
- +2 more
Oct 24, 2022
Diamond Blackfan Anemia Trial in Manhasset (Sotatercept, Sotatercept with prednisone boost)
Terminated
- Diamond Blackfan Anemia
- Sotatercept
- Sotatercept with prednisone boost
-
Manhasset, New YorkNorth Shore- LIJ campus of The Feinstein Institute for Medical R
Nov 22, 2021
Aplastic Anemia, Pure Red Cell Aplasia, Diamond Blackfan Anemia Trial run by the NHLBI (Daclizumab)
Terminated
- Aplastic Anemia
- +2 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center, 9000 Rockville Pi
Jun 15, 2021
Bone Marrow Failure Syndrome, Severe Aplastic Anemia, Severe Congenital Neutropenia Trial in New York (CD34 Stem Cell Selection
Active, not recruiting
- Bone Marrow Failure Syndrome
- +15 more
- CD34 Stem Cell Selection Therapy
-
New York, New YorkMorgan Stanley Children's Hospital, New York-Presbyterian, Colum
Jun 17, 2020
Severe Aplastic Anemia Who Developed High Risk Clonal Evolution
Completed
- Severe Aplastic Anemia
-
Bethesda, MarylandNational Heart, Lung and Blood Institute (NHLBI)
Apr 7, 2022
Sickle Cell Anemia, Beta-thalassemia Major, Diamond-blackfan Anemia Trial in Pittsburgh (CD3/CD19 depleted leukocytes, CD45RA
Recruiting
- Sickle Cell Anemia
- +2 more
- CD3/CD19 depleted leukocytes
- +6 more
-
Pittsburgh, PennsylvaniaChildren's Hospital of Pittsburgh of UPMC
May 4, 2022
Hurler Syndrome, Fanconi Anemia, Glanzmann Thrombasthenia Trial in Atlanta (Abatacept)
Completed
- Hurler Syndrome
- +14 more
-
Atlanta, GeorgiaChildren's Healthcare of Atlanta
Dec 20, 2019
Baby Detect : Genomic Newborn Screening
Recruiting
- Congenital Adrenal Hyperplasia
- +126 more
-
Liege, Wallonia, BelgiumCRMN, Hôpital La Citadelle
Jan 24, 2023
Acquired and Inherited Bone Marrow Failure Syndromes
Recruiting
- Severe Aplastic Anemia
- +2 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Aug 12, 2022
Familial Investigations of Childhood Cancer Predisposition
Recruiting
- Acute Leukemia
- +45 more
-
Memphis, TennesseeSt. Jude Children's Research Hospital
May 11, 2022
Acute Leukemia, Immune Deficiency Disorder, Congenital Hematological Disorder Trial in Rochester (radiation, drug, procedure)
Recruiting
- Acute Leukemia
- +9 more
- Total Body Irradiation 1200 cGy
- +7 more
-
Rochester, New YorkWilmot Cancer Institute
Jun 20, 2022
Bone Marrow Failure Syndromes Trial in Philadelphia (MRD-BMT with Fludarabine-based RIC for Acquired AA, MRD-BMT with
Recruiting
- Bone Marrow Failure Syndromes
- MRD-BMT with Fludarabine-based RIC for Acquired AA
- +2 more
-
Philadelphia, PennsylvaniaChildren's Hospital of Philadelphia
May 6, 2022
Acquired Aplastic Anemia, Paroxysmal Nocturnal Hemoglobinuria, Inherited Bone Marrow Failure Syndromes Trial in Philadelphia
Recruiting
- Acquired Aplastic Anemia
- +2 more
- CliniMACs
-
Philadelphia, PennsylvaniaChildren's Hospital of Philadelphia
Mar 1, 2022
Bone Marrow Failure Syndrome, Thalassemia, Sickle Cell Disease Trial in Gainesville (Thiotepa--single daily dose,
Recruiting
- Bone Marrow Failure Syndrome
- +15 more
- Thiotepa--single daily dose
- Thiotepa--escalated dose
-
Gainesville, FloridaUF Health Shands Children's Hospital
Jul 8, 2021
Bone Marrow Failure Syndrome, Congenital Amegakaryocytic Thrombocytopenia, Congenital Pure Red Cell Aplasia Trial in United
Recruiting
- Bone Marrow Failure Syndrome
- +6 more
- Treosulfan
- +7 more
-
Los Angeles, California
- +23 more
Aug 15, 2022
Multi-Center Study of Iron Overload: Survey Study (MCSIO)
Completed
- Sickle Cell Disease
- +2 more
-
Oakland, California
- +7 more
Sep 22, 2020
Multi-Center Study of Iron Overload: Pilot Study
Completed
- Sickle Cell Disease
- +2 more
-
Oakland, California
- +2 more
Sep 22, 2020
Accelerated Phase Chronic Myelogenous Leukemia, Adult Acute Lymphoblastic Leukemia in Remission, Adult Acute Myeloid Leukemia in
Completed
- Accelerated Phase Chronic Myelogenous Leukemia
- +77 more
- fludarabine phosphate
- +8 more
-
Buffalo, New YorkRoswell Park Cancer Institute
Sep 16, 2019
Congenital Hemolytic Anemia, Sickle Cell Disease Trial run by the National Heart, Lung, and Blood Institute (NHLBI) (Peripheral
Recruiting
- Congenital Hemolytic Anemia
- Sickle Cell Disease
- Peripheral blood hematopoietic progenitor cell (PBPC) transplant
- +3 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 25, 2023
